From 2021, patients suffering from RPE65-associated retinal disease will be able to be treated in three UMCs of the Netherlands.
https://www.radboudumc.nl/nieuws/2020/gentherapie-voor-zeldzame-oogziekte-vergoed
From 2021, patients suffering from RPE65-associated retinal disease will be able to be treated in three UMCs of the Netherlands.
https://www.radboudumc.nl/nieuws/2020/gentherapie-voor-zeldzame-oogziekte-vergoed
Scientists from Trinity College Dublin have developed a new gene therapy approach that offers promise for one day treating an eye disease that leads to a progressive loss of vision and affects thousands of people across the globe. The study, which involved a collaboration with clinical teams in the Royal Victoria Eye and Ear Hospital and the Mater Hospital, also has implications for a much wider suite of neurological disorders associated with ageing.
Source: Scientists develop new gene therapy for eye disease | EurekAlert! Science News
The Nobel Prize in Chemistry 2020 was awarded jointly to Emmanuelle Charpentier and Jennifer A. Doudna “for the development of a method for genome editing”.
Prof. Dr. Alessandro Aiuti, a physician and research scientist based in Milan is the winner of the Else Kröner Fresenius Prize for Medical Research 2020, which is awarded by the EKFS in recognition of Aiuti’s significant scientific contributions to the development of gene therapies.
Source: Else Kröner Fresenius Prize for Medical Research 2020 | Else Kröner-Fresenius-Stiftung