Posted on 19/03/202119/03/2021Sarepta Therapeutics’ Investigational Gene Therapy SRP-9003 for the Treatment of Limb-Girdle Muscular Dystrophy Type 2E Shows Sustained Expression and Functional Improvements 2 Years After Administration
Posted on 19/03/202119/03/2021Translate Bio Announces Results from Second Interim Data Analysis from Ongoing Phase 1/2 Clinical Trial of MRT5005 in Patients with Cystic Fibrosis (CF)
Posted on 16/03/202116/03/2021Solid Biosciences Reports Efficacy and Safety Data from the Ongoing IGNITE DMD Clinical Trial https://investors.solidbio.com/news-releases/news-release-details/solid-biosciences-reports-efficacy-and-safety-data-ongoing
Posted on 13/03/202113/03/2021bluebird bio announces that lentiviral vector BB305 is unlikely to be the cause of AML in clinical study of LentiGlobin for Sickle Cell Disease 4 4 https://investor.bluebirdbio.com/news-releases/news-release-details/bluebird-bio-provides-updated-findings-reported-case-acute